Search for Clinical Trial Results
Leukodystrophy, Metachromatic - 25 Studies Found
Status | Study |
Recruiting |
Study Name: Autologous Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy and Adrenoleukodystrophy Condition:
Date: 2015-08-12 Interventions: Genetic: transduced CD34+ hematopoietic stem cell Autologous hematopoietic stem cells (HSCs) collected f |
No longer available |
Study Name: Single Patient Expanded Access Protocol: Metabolic Boost Condition: Metachromatic Leukodystrophy Date: 2013-12-19 Interventions: Biological: Enriched Hematopoetic Stem Cell Infusion Enriched Hematopoetic Stem Cell Infusion |
No longer available |
Study Name: Allogeneic Stem Cell Transplantation for the Treatment of Multiple Sclerosis (Compassionate Use) Condition: Metachromatic Leukodystrophy Date: 2014-03-07 Interventions: Biological: Enriched Hematopoetic Stem Cell Infusion Enriched Hematopoetic Stem Cell Infusion |
Recruiting |
Study Name: Biomarker for Metachromatic Leukodystrophy Disease Condition:
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Active, not recruiting |
Study Name: Gene Therapy for Metachromatic Leukodystrophy Condition: Lysosomal Storage Disease Date: 2012-03-16 Interventions: Genetic: Autologous CD34+ stem cells transduced with ARSA encoding lentiviral vector Autologous hematopo |
Terminated |
Study Name: Natural History Study of Children With Metachromatic Leukodystrophy Condition:
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Recruiting |
Study Name: UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells Condition:
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Completed |
Study Name: Stem Cell Transplantation (SCT) for Genetic Diseases Condition:
Interventions: |
Completed |
Study Name: Study of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoietic Stem Cell Transplantation Condition:
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